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Genome Editing and Muscle Stem Cells as a Therapeutic Tool for Muscular Dystrophies

PURPOSE OF REVIEW: Muscular dystrophies are a group of severe degenerative disorders characterized by muscle fiber degeneration and death. Therapies designed to restore muscle homeostasis and to replace dying fibers are being experimented, but none of those in clinical trials are suitable to permane...

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Detalles Bibliográficos
Autores principales: Pini, Veronica, Morgan, Jennifer E., Muntoni, Francesco, O’Neill, Helen C.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer International Publishing 2017
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5445179/
https://www.ncbi.nlm.nih.gov/pubmed/28616376
http://dx.doi.org/10.1007/s40778-017-0076-6