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Myogenic differentiation of VCP disease-induced pluripotent stem cells: A novel platform for drug discovery
Valosin Containing Protein (VCP) disease is an autosomal dominant multisystem proteinopathy caused by mutations in the VCP gene, and is primarily associated with progressive muscle weakness, including atrophy of the pelvic and shoulder girdle muscles. Currently, no treatments are available and cardi...
Autores principales: | , , , , , , , , |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Public Library of Science
2017
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5456028/ https://www.ncbi.nlm.nih.gov/pubmed/28575052 http://dx.doi.org/10.1371/journal.pone.0176919 |