Retrospective study of long-term outcomes of enzyme replacement therapy in Fabry disease: Analysis of prognostic factors

Despite enzyme replacement therapy, disease progression is observed in patients with Fabry disease. Identification of factors that predict disease progression is needed to refine guidelines on initiation and cessation of enzyme replacement therapy. To study the association of potential biochemical a...

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Detalles Bibliográficos
Autores principales: Arends, Maarten, Biegstraaten, Marieke, Hughes, Derralynn A., Mehta, Atul, Elliott, Perry M., Oder, Daniel, Watkinson, Oliver T., Vaz, Frédéric M., van Kuilenburg, André B. P., Wanner, Christoph, Hollak, Carla E. M.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Public Library of Science 2017
Materias:
Research Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5538714/
https://www.ncbi.nlm.nih.gov/pubmed/28763515
http://dx.doi.org/10.1371/journal.pone.0182379

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5538714/
https://www.ncbi.nlm.nih.gov/pubmed/28763515
http://dx.doi.org/10.1371/journal.pone.0182379

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