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Retrospective study of long-term outcomes of enzyme replacement therapy in Fabry disease: Analysis of prognostic factors
Despite enzyme replacement therapy, disease progression is observed in patients with Fabry disease. Identification of factors that predict disease progression is needed to refine guidelines on initiation and cessation of enzyme replacement therapy. To study the association of potential biochemical a...
Autores principales: | Arends, Maarten, Biegstraaten, Marieke, Hughes, Derralynn A., Mehta, Atul, Elliott, Perry M., Oder, Daniel, Watkinson, Oliver T., Vaz, Frédéric M., van Kuilenburg, André B. P., Wanner, Christoph, Hollak, Carla E. M. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Public Library of Science
2017
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5538714/ https://www.ncbi.nlm.nih.gov/pubmed/28763515 http://dx.doi.org/10.1371/journal.pone.0182379 |
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