Long-term outcomes with agalsidase alfa enzyme replacement therapy: Analysis using deconstructed composite events

This is a retrospective analysis of Fabry Outcome Survey data from children/adults (n = 677) receiving agalsidase alfa enzyme replacement therapy for a median of 3 years, examining cerebrovascular, cardiac, and renal morbidity endpoints separately. Cardiac events occurred at younger ages than cerebr...

Descripción completa

Detalles Bibliográficos
Autores principales: Beck, Michael, Hughes, Derralynn, Kampmann, Christoph, Pintos-Morell, Guillem, Ramaswami, Uma, West, Michael L., Giugliani, Roberto
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Elsevier 2017
Materias:
Short Communication
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5684503/
https://www.ncbi.nlm.nih.gov/pubmed/29159077
http://dx.doi.org/10.1016/j.ymgmr.2017.10.008

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5684503/
https://www.ncbi.nlm.nih.gov/pubmed/29159077
http://dx.doi.org/10.1016/j.ymgmr.2017.10.008

Ejemplares similares