Striated muscle gene therapy for the treatment of lipoprotein lipase deficiency

Excessive circulating triglycerides due to reduction or loss of lipoprotein lipase activity contribute to hypertriglyceridemia and increased risk for pancreatitis. The only gene therapy treatment for lipoprotein lipase deficiency decreases pancreatitis but minimally reduces hypertriglyceridemia. Syn...

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Detalles Bibliográficos
Autores principales: Gadek, Katherine E., Wang, Hong, Hall, Monica N., Sungello, Mitchell, Libby, Andrew, MacLaskey, Drew, Eckel, Robert H., Olwin, Bradley B.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Public Library of Science 2018
Materias:
Research Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5755938/
https://www.ncbi.nlm.nih.gov/pubmed/29304082
http://dx.doi.org/10.1371/journal.pone.0190963

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5755938/
https://www.ncbi.nlm.nih.gov/pubmed/29304082
http://dx.doi.org/10.1371/journal.pone.0190963

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