Allele‐specific silencing therapy for Dynamin 2‐related dominant centronuclear myopathy

Rapid advances in allele‐specific silencing by RNA interference established a strategy of choice to cure dominant inherited diseases by targeting mutant alleles. We used this strategy for autosomal‐dominant centronuclear myopathy (CNM), a rare neuromuscular disorder without available treatment due t...

Descripción completa

Detalles Bibliográficos
Autores principales: Trochet, Delphine, Prudhon, Bernard, Beuvin, Maud, Peccate, Cécile, Lorain, Stéphanie, Julien, Laura, Benkhelifa‐Ziyyat, Sofia, Rabai, Aymen, Mamchaoui, Kamel, Ferry, Arnaud, Laporte, Jocelyn, Guicheney, Pascale, Vassilopoulos, Stéphane, Bitoun, Marc
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2017
Materias:
Research Articles
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5801507/
https://www.ncbi.nlm.nih.gov/pubmed/29246969
http://dx.doi.org/10.15252/emmm.201707988

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5801507/
https://www.ncbi.nlm.nih.gov/pubmed/29246969
http://dx.doi.org/10.15252/emmm.201707988

Ejemplares similares