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Analysis of phase II methodologies for single-arm clinical trials with multiple endpoints in rare cancers: An example in Ewing’s sarcoma

Trials run in either rare diseases, such as rare cancers, or rare sub-populations of common diseases are challenging in terms of identifying, recruiting and treating sufficient patients in a sensible period. Treatments for rare diseases are often designed for other disease areas and then later propo...

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Detalles Bibliográficos
Autores principales: Dutton, P, Love, SB, Billingham, L, Hassan, AB
Formato: Online Artículo Texto
Lenguaje:English
Publicado: SAGE Publications 2016
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5863794/
https://www.ncbi.nlm.nih.gov/pubmed/27587590
http://dx.doi.org/10.1177/0962280216662070