Pompe disease treatment with twice a week high dose alglucoside alfa in a patient with severe dilated cardiomyopathy

There is limited information regarding ideal dosage of alglucoside alfa in patients with Infantile Onset Pompe Disease (IOPD). The U.S. Food and Drug Administration approved alglucoside alfa at dosing of 20 mg/kg every other week, but there are small studies and case reports suggesting that dosing h...

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Detalles Bibliográficos
Autores principales: Landis, Jesa L., Hyland, Holly, Kindel, Steven J., Punnoose, Ann, Geddes, Gabrielle C.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Elsevier 2018
Materias:
Case Report
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6014588/
https://www.ncbi.nlm.nih.gov/pubmed/29946513
http://dx.doi.org/10.1016/j.ymgmr.2018.05.002

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6014588/
https://www.ncbi.nlm.nih.gov/pubmed/29946513
http://dx.doi.org/10.1016/j.ymgmr.2018.05.002

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