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Pompe disease treatment with twice a week high dose alglucoside alfa in a patient with severe dilated cardiomyopathy
There is limited information regarding ideal dosage of alglucoside alfa in patients with Infantile Onset Pompe Disease (IOPD). The U.S. Food and Drug Administration approved alglucoside alfa at dosing of 20 mg/kg every other week, but there are small studies and case reports suggesting that dosing h...
| Autores principales: | , , , , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
| Publicado: |
Elsevier
2018
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| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6014588/ https://www.ncbi.nlm.nih.gov/pubmed/29946513 http://dx.doi.org/10.1016/j.ymgmr.2018.05.002 |