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Sirolimus in Infants with Multiple Cardiac Rhabdomyomas Associated with Tuberous Sclerosis Complex

INTRODUCTION: Cardiac rhabdomyomas represent a frequent manifestation of tuberous sclerosis. Tumor growth, mainly prenatally, can result in intrauterine fetal or neonatal deaths in almost 10% of patients. CASE REPORT: We treated 3 consecutive infants aged less than 12 months with sirolimus, an oral...

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Detalles Bibliográficos
Autores principales: Lucchesi, Maurizio, Chiappa, Enrico, Giordano, Flavio, Mari, Francesco, Genitori, Lorenzo, Sardi, Iacopo
Formato: Online Artículo Texto
Lenguaje:English
Publicado: S. Karger AG 2018
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6062714/
https://www.ncbi.nlm.nih.gov/pubmed/30057537
http://dx.doi.org/10.1159/000490662