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Gene editing: A new step and a new direction toward finding a cure for Duchenne muscular dystrophy (DMD)

Duchenne muscular dystrophy (DMD) is a progressive muscle degenerative disease affecting one out of 3500 male births. Patients usually succumb to the disease by age 25. It has been shown that skipping exons of the DMD gene that contain disease-causing mutations from the pre-mRNA can result in a shor...

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Detalles Bibliográficos
Autores principales: Hu, Jim, Xia, Emily, Yang, Leo, Xiao, Xiao
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Chongqing Medical University 2016
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6146171/
https://www.ncbi.nlm.nih.gov/pubmed/30258878
http://dx.doi.org/10.1016/j.gendis.2016.02.001