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Transplantation, gene therapy and intestinal pathology in MNGIE patients and mice

BACKGROUND: Gastrointestinal complications are the main cause of death in patients with mitochondrial neurogastrointestinal encephalomyopathy (MNGIE). Available treatments often restore biochemical homeostasis, but fail to cure gastrointestinal symptoms. METHODS: We evaluated the small intestine neu...

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Detalles Bibliográficos
Autores principales:	Yadak, Rana, Boot, Max V., van Til, Niek P., Cazals-Hatem, Dominique, Finkenstedt, Armin, Bogaerts, Elly, de Coo, Irenaeus F., Bugiani, Marianna
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2018
Materias:	Research Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6194683/ https://www.ncbi.nlm.nih.gov/pubmed/30340467 http://dx.doi.org/10.1186/s12876-018-0881-0

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