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Cystic Fibrosis Gene Therapy: Looking Back, Looking Forward

Cystic fibrosis (CF) is an autosomal recessive disease caused by mutations in the cystic fibrosis transmembrane conductance regulator (CFTR) gene that encodes a cAMP-regulated anion channel. Although CF is a multi-organ system disease, most people with CF die of progressive lung disease that begins...

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Detalles Bibliográficos
Autores principales: Cooney, Ashley L., McCray, Paul B., Sinn, Patrick L.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2018
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6266271/
https://www.ncbi.nlm.nih.gov/pubmed/30405068
http://dx.doi.org/10.3390/genes9110538