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Clinical Trial Designs and Measures in Hereditary Spastic Paraplegias

Hereditary spastic paraplegias (HSPs) are a large group of genetically-diverse neurologic disorders characterized clinically by a common feature of lower extremity spasticity and gait difficulties. Current therapies are predominantly symptomatic, and even then usually provide inadequate relief of sy...

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Detalles Bibliográficos
Autores principales:	Trummer, Brian, Haubenberger, Dietrich, Blackstone, Craig
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Frontiers Media S.A. 2018
Materias:	Neurology
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6309810/ https://www.ncbi.nlm.nih.gov/pubmed/30627115 http://dx.doi.org/10.3389/fneur.2018.01017

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