Applications of CRISPR/Cas9 for the Treatment of Duchenne Muscular Dystrophy

Duchenne muscular dystrophy (DMD) is a fatal X-linked recessive neuromuscular disease prevalent in 1 in 3500 to 5000 males worldwide. As a result of mutations that interrupt the reading frame of the dystrophin gene (DMD), DMD is characterized by a loss of dystrophin protein that leads to decreased m...

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Detalles Bibliográficos
Autores principales: Lim, Kenji Rowel Q., Yoon, Chantal, Yokota, Toshifumi
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2018
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6313657/
https://www.ncbi.nlm.nih.gov/pubmed/30477208
http://dx.doi.org/10.3390/jpm8040038

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6313657/
https://www.ncbi.nlm.nih.gov/pubmed/30477208
http://dx.doi.org/10.3390/jpm8040038

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