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Amifampridine Phosphate (Firdapse) Is Effective in a Confirmatory Phase 3 Clinical Trial in LEMS

OBJECTIVE: To assess tolerability and efficacy of amifampridine phosphate versus placebo for symptomatic treatment of Lambert–Eaton Myasthenic Syndrome (LEMS). METHODS: This phase 3 randomized, double-blind, placebo-controlled withdrawal trial in 26 adults with LEMS compared efficacy of amifampridin...

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Detalles Bibliográficos
Autores principales: Shieh, Perry, Sharma, Khema, Kohrman, Bruce, Oh, Shin J.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Journal of Clinical Neuromuscular Disease 2019
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6392213/
https://www.ncbi.nlm.nih.gov/pubmed/30801481
http://dx.doi.org/10.1097/CND.0000000000000239