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Amifampridine Phosphate (Firdapse) Is Effective in a Confirmatory Phase 3 Clinical Trial in LEMS
OBJECTIVE: To assess tolerability and efficacy of amifampridine phosphate versus placebo for symptomatic treatment of Lambert–Eaton Myasthenic Syndrome (LEMS). METHODS: This phase 3 randomized, double-blind, placebo-controlled withdrawal trial in 26 adults with LEMS compared efficacy of amifampridin...
Autores principales: | Shieh, Perry, Sharma, Khema, Kohrman, Bruce, Oh, Shin J. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Journal of Clinical Neuromuscular Disease
2019
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6392213/ https://www.ncbi.nlm.nih.gov/pubmed/30801481 http://dx.doi.org/10.1097/CND.0000000000000239 |
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