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Rare Opportunities: CRISPR/Cas-Based Therapy Development for Rare Genetic Diseases

Rare diseases pose a global challenge, in that their collective impact on health systems is considerable, whereas their individually rare occurrence impedes research and development of efficient therapies. In consequence, patients and their families are often unable to find an expert for their affli...

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Detalles Bibliográficos
Autores principales: Papasavva, Panayiota, Kleanthous, Marina, Lederer, Carsten W.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer International Publishing 2019
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6469594/
https://www.ncbi.nlm.nih.gov/pubmed/30945166
http://dx.doi.org/10.1007/s40291-019-00392-3