Gene therapy as a potential therapeutic option for Duchenne muscular dystrophy: A qualitative preference study of patients and parents

OBJECTIVES: Duchenne muscular dystrophy (DMD) is a rare neuromuscular disorder that causes progressive weakness and early death. Gene therapy is an area of new therapeutic development. This qualitative study explored factors influencing parents’ and adult patients’ preferences about gene therapy. ME...

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Detalles Bibliográficos
Autores principales: Landrum Peay, Holly, Fischer, Ryan, Tzeng, Janice P., Hesterlee, Sharon E., Morris, Carl, Strong Martin, Amy, Rensch, Colin, Smith, Edward, Ricotti, Valeria, Beaverson, Katherine, Wand, Hannah, Mansfield, Carol
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Public Library of Science 2019
Materias:
Research Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6493713/
https://www.ncbi.nlm.nih.gov/pubmed/31042754
http://dx.doi.org/10.1371/journal.pone.0213649

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6493713/
https://www.ncbi.nlm.nih.gov/pubmed/31042754
http://dx.doi.org/10.1371/journal.pone.0213649

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