Inotersen: new promise for the treatment of hereditary transthyretin amyloidosis

Hereditary transthyretin amyloidosis is a fatal autosomal dominant disorder characterized by deposition of transthyretin amyloid into the peripheral nervous system, heart, kidney, and gastrointestinal tract. Previous treatments using liver transplantation and small molecule stabilizers were not effe...

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Detalles Bibliográficos
Autores principales: Mathew, Veena, Wang, Annabel K
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Dove Medical Press 2019
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6507904/
https://www.ncbi.nlm.nih.gov/pubmed/31118583
http://dx.doi.org/10.2147/DDDT.S162913

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6507904/
https://www.ncbi.nlm.nih.gov/pubmed/31118583
http://dx.doi.org/10.2147/DDDT.S162913

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