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Genome Editing as a Treatment for the Most Prevalent Causative Genes of Autosomal Dominant Retinitis Pigmentosa

Inherited retinal dystrophies (IRDs) are a clinically and genetically heterogeneous group of diseases with more than 250 causative genes. The most common form is retinitis pigmentosa. IRDs lead to vision impairment for which there is no universal cure. Encouragingly, a first gene supplementation the...

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Detalles Bibliográficos
Autores principales: Diakatou, Michalitsa, Manes, Gaël, Bocquet, Beatrice, Meunier, Isabelle, Kalatzis, Vasiliki
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2019
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6567127/
https://www.ncbi.nlm.nih.gov/pubmed/31126147
http://dx.doi.org/10.3390/ijms20102542