Effects of gene therapy on cardiovascular symptoms of lysosomal storage diseases

Lysosomal storage diseases (LSDs) are inherited conditions caused by impaired lysosomal function and consequent substrate storage, leading to a range of clinical manifestations, including cardiovascular disease. This may lead to significant symptoms and even cardiac failure, which is an important ca...

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Detalles Bibliográficos
Autores principales: Poletto, Edina, Pasqualim, Gabriela, Giugliani, Roberto, Matte, Ursula, Baldo, Guilherme
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Sociedade Brasileira de Genética 2019
Materias:
Articles
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6687348/
https://www.ncbi.nlm.nih.gov/pubmed/31132295
http://dx.doi.org/10.1590/1678-4685-GMB-2018-0100

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6687348/
https://www.ncbi.nlm.nih.gov/pubmed/31132295
http://dx.doi.org/10.1590/1678-4685-GMB-2018-0100

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