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Effects of gene therapy on cardiovascular symptoms of lysosomal storage diseases

Lysosomal storage diseases (LSDs) are inherited conditions caused by impaired lysosomal function and consequent substrate storage, leading to a range of clinical manifestations, including cardiovascular disease. This may lead to significant symptoms and even cardiac failure, which is an important ca...

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Detalles Bibliográficos
Autores principales:	Poletto, Edina, Pasqualim, Gabriela, Giugliani, Roberto, Matte, Ursula, Baldo, Guilherme
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Sociedade Brasileira de Genética 2019
Materias:	Articles
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6687348/ https://www.ncbi.nlm.nih.gov/pubmed/31132295 http://dx.doi.org/10.1590/1678-4685-GMB-2018-0100

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