Cargando…

Advances in the treatment of hereditary transthyretin amyloidosis: A review

INTRODUCTION: Amyloid transthyretin amyloidosis (ATTR) is a progressive and often fatal disease caused by the buildup of mutated (hereditary ATTR [hATTR]; also known as ATTR variant [ATTRv]) or normal transthyretin (wild‐type ATTR) throughout the body. Two new therapies—inotersen, an antisense oligo...

Descripción completa

Detalles Bibliográficos
Autores principales: Gertz, Morie A., Mauermann, Michelle L., Grogan, Martha, Coelho, Teresa
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2019
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6749475/
https://www.ncbi.nlm.nih.gov/pubmed/31368669
http://dx.doi.org/10.1002/brb3.1371