A randomized pilot efficacy and safety trial of diazoxide choline controlled-release in patients with Prader-Willi syndrome

INTRODUCTION: Prader-Willi syndrome (PWS) is a complex genetic condition characterized by hyperphagia, hypotonia, low muscle mass, excess body fat, developmental delays, intellectual disability, behavioral problems, and growth hormone deficiency. This study evaluated the safety and efficacy of orall...

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Detalles Bibliográficos
Autores principales: Kimonis, Virginia, Surampalli, Abhilasha, Wencel, Marie, Gold, June-Anne, Cowen, Neil M.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Public Library of Science 2019
Materias:
Research Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6756513/
https://www.ncbi.nlm.nih.gov/pubmed/31545799
http://dx.doi.org/10.1371/journal.pone.0221615

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6756513/
https://www.ncbi.nlm.nih.gov/pubmed/31545799
http://dx.doi.org/10.1371/journal.pone.0221615

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