Molecular Therapies for Inherited Retinal Diseases—Current Standing, Opportunities and Challenges

Inherited retinal diseases (IRDs) are both genetically and clinically highly heterogeneous and have long been considered incurable. Following the successful development of a gene augmentation therapy for biallelic RPE65-associated IRD, this view has changed. As a result, many different therapeutic a...

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Detalles Bibliográficos
Autores principales: Vázquez-Domínguez, Irene, Garanto, Alejandro, Collin, Rob W. J.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2019
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6770110/
https://www.ncbi.nlm.nih.gov/pubmed/31466352
http://dx.doi.org/10.3390/genes10090654

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6770110/
https://www.ncbi.nlm.nih.gov/pubmed/31466352
http://dx.doi.org/10.3390/genes10090654

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