Gene Therapy for ALS—A Perspective

Amyotrophic lateral sclerosis (ALS) is a fatal motor neuron disease (MND) with no cure. Recent advances in gene therapy open a new perspective to treat this disorder—particularly for the characterized genetic forms. Gene therapy approaches, involving the delivery of antisense oligonucleotides into t...

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Detalles Bibliográficos
Autores principales: Cappella, Marisa, Ciotti, Chiara, Cohen-Tannoudji, Mathilde, Biferi, Maria Grazia
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2019
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6771059/
https://www.ncbi.nlm.nih.gov/pubmed/31500113
http://dx.doi.org/10.3390/ijms20184388

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6771059/
https://www.ncbi.nlm.nih.gov/pubmed/31500113
http://dx.doi.org/10.3390/ijms20184388

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