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Gene Therapy for ALS—A Perspective
Amyotrophic lateral sclerosis (ALS) is a fatal motor neuron disease (MND) with no cure. Recent advances in gene therapy open a new perspective to treat this disorder—particularly for the characterized genetic forms. Gene therapy approaches, involving the delivery of antisense oligonucleotides into t...
Autores principales: | Cappella, Marisa, Ciotti, Chiara, Cohen-Tannoudji, Mathilde, Biferi, Maria Grazia |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2019
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6771059/ https://www.ncbi.nlm.nih.gov/pubmed/31500113 http://dx.doi.org/10.3390/ijms20184388 |
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