Cargando…
Clinical Considerations for Capsid Choice in the Development of Liver-Targeted AAV-Based Gene Transfer
As gene transfer with adeno-associated virus (AAV) vectors is starting to enter clinical practice, this review examines the impact of vector capsid choice in liver-directed gene transfer for hemophilia. Given that there are multiple clinical trials completed and ongoing in this field, it is importan...
| Autores principales: | , , , , |
|---|---|
| Formato: | Online Artículo Texto |
| Lenguaje: | English |
| Publicado: |
American Society of Gene & Cell Therapy
2019
|
| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6807344/ https://www.ncbi.nlm.nih.gov/pubmed/31660419 http://dx.doi.org/10.1016/j.omtm.2019.08.015 |