Estimation Of The Quality Of Life Benefits Associated With Treatment For Spinal Muscular Atrophy

BACKGROUND: Spinal muscular atrophy (SMA) is a rare, genetic, progressive neuromuscular disorder characterized by severe muscle atrophy and weakness and is a leading genetic cause of death in infants and children. Nusinersen was the first treatment targeting the underlying cause of disease approved...

Descripción completa

Detalles Bibliográficos
Autores principales: Lloyd, Andrew J, Thompson, Robin, Gallop, Katy, Teynor, Megan
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Dove 2019
Materias:
Original Research
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6818531/
https://www.ncbi.nlm.nih.gov/pubmed/31749625
http://dx.doi.org/10.2147/CEOR.S214084

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6818531/
https://www.ncbi.nlm.nih.gov/pubmed/31749625
http://dx.doi.org/10.2147/CEOR.S214084

Ejemplares similares