Hematopoietic Stem Cell Transplantation in Inborn Errors of Metabolism

Hematopoietic stem cell transplantation (HSCT) has been established as an effective therapy for selected inborn errors of metabolism. The success of HSCT in metabolic disease is best exemplified through the treatment of Hurler's syndrome, a lysosomal storage disease. Through the collaborative e...

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Detalles Bibliográficos
Autores principales: Tan, Emily Y., Boelens, Jaap Jan, Jones, Simon A., Wynn, Robert F.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2019
Materias:
Pediatrics
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6824291/
https://www.ncbi.nlm.nih.gov/pubmed/31709204
http://dx.doi.org/10.3389/fped.2019.00433

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6824291/
https://www.ncbi.nlm.nih.gov/pubmed/31709204
http://dx.doi.org/10.3389/fped.2019.00433

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