Autologous Stem-Cell-Based Gene Therapy for Inherited Disorders: State of the Art and Perspectives

Gene therapy using patient's own stem cells is rapidly becoming an alternative to allogeneic stem cell transplantation, especially when suitably compatible donors cannot be found. The advent of efficient virus-based methods for delivering therapeutic genes has enabled the development of genetic...

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Detalles Bibliográficos
Autores principales: Staal, Frank J. T., Aiuti, Alessandro, Cavazzana, Marina
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2019
Materias:
Pediatrics
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6834641/
https://www.ncbi.nlm.nih.gov/pubmed/31737588
http://dx.doi.org/10.3389/fped.2019.00443

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6834641/
https://www.ncbi.nlm.nih.gov/pubmed/31737588
http://dx.doi.org/10.3389/fped.2019.00443

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