Metachromatic leukodystrophy and transplantation: remyelination, no cross‐correction

OBJECTIVE: In metachromatic leukodystrophy, a lysosomal storage disorder due to decreased arylsulfatase A activity, hematopoietic stem cell transplantation may stop brain demyelination and allow remyelination, thereby halting white matter degeneration. This is the first study to define the effects a...

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Detalles Bibliográficos
Autores principales: Wolf, Nicole I., Breur, Marjolein, Plug, Bonnie, Beerepoot, Shanice, Westerveld, Aimee S. R., van Rappard, Diane F., de Vries, Sharon I., Kole, Maarten H. P., Vanderver, Adeline, van der Knaap, Marjo S., Lindemans, Caroline A., van Hasselt, Peter M., Boelens, Jaap J., Matzner, Ulrich, Gieselmann, Volkmar, Bugiani, Marianna
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2020
Materias:
Research Articles
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7034505/
https://www.ncbi.nlm.nih.gov/pubmed/31967741
http://dx.doi.org/10.1002/acn3.50975

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7034505/
https://www.ncbi.nlm.nih.gov/pubmed/31967741
http://dx.doi.org/10.1002/acn3.50975

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