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The safety and effectiveness of chenodeoxycholic acid treatment in patients with cerebrotendinous xanthomatosis: two retrospective cohort studies

OBJECTIVE: To evaluate the safety and effectiveness of chenodeoxycholic acid (CDCA) treatment in patients with cerebrotendinous xanthomatosis (CTX). METHODS: Two retrospective cohort studies were conducted in CTX patients who underwent CDCA treatment: one in the Netherlands (NL; CDCA-STUK-15-001) an...

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Detalles Bibliográficos
Autores principales: Verrips, Aad, Dotti, Maria Teresa, Mignarri, Andrea, Stelten, Bianca M. L., Verma, Sue, Federico, Antonio
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer International Publishing 2019
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7160076/
https://www.ncbi.nlm.nih.gov/pubmed/31863326
http://dx.doi.org/10.1007/s10072-019-04169-8