Failure of intrathecal allogeneic mesenchymal stem cells to halt progressive demyelination in two boys with cerebral adrenoleukodystrophy

Cerebral adrenoleukodystrophy is an inflammatory demyelinating condition that is the result of a mutation in the X‐linked ABCD1 gene, a peroxisomal very long chain fatty acid transporter. Although mutations in this gene result in adrenal insufficiency in the majority of affected individuals, 40% of...

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Detalles Bibliográficos
Autores principales: Gupta, Ashish, Orchard, Paul J., Miller, Weston P., Nascene, Dave R., Raymond, Gerald V., Loes, Daniel J., McKenna, David H., Lund, Troy C.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley & Sons, Inc. 2020
Materias:
Human Clinical Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7180290/
https://www.ncbi.nlm.nih.gov/pubmed/32020747
http://dx.doi.org/10.1002/sctm.19-0304

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7180290/
https://www.ncbi.nlm.nih.gov/pubmed/32020747
http://dx.doi.org/10.1002/sctm.19-0304

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