Conditions for combining gene therapy with bone marrow transplantation in murine Krabbe disease

[Image: see text] Introduction: Krabbe disease (KD) is an autosomal recessive lysosomal disorder caused by mutations in the galactocerebrosidase (GALC) gene. This results in defective myelination in the peripheral and central nervous systems due to low GALC activity. Treatment at this time is limite...

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Detalles Bibliográficos
Autores principales: Rafi, Mohammad A., Luzi, Paola, Wenger, David A.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Tabriz University of Medical Sciences 2020
Materias:
Original Research
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7186542/
https://www.ncbi.nlm.nih.gov/pubmed/32363154
http://dx.doi.org/10.34172/bi.2020.13

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7186542/
https://www.ncbi.nlm.nih.gov/pubmed/32363154
http://dx.doi.org/10.34172/bi.2020.13

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