Development of the pyruvate kinase deficiency diary and pyruvate kinase deficiency impact assessment: Disease‐specific assessments

INTRODUCTION: Currently recommended patient‐reported outcome (PRO) measures for patients with pyruvate kinase (PK) deficiency are non‐disease‐specific. The PK Deficiency Diary (PKDD) and PK Deficiency Impact Assessment (PKDIA) were developed to be more targeted measures for capturing the symptoms an...

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Detalles Bibliográficos
Autores principales: Salek, Sam, Boscoe, Audra N., Piantedosi, Sarah, Egan, Shayna, Evans, Christopher J, Wells, Ted, Cohen, Jennifer, Klaassen, Robert J., Grace, Rachael, Storm, Michael
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2020
Materias:
Original Articles
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7216839/
https://www.ncbi.nlm.nih.gov/pubmed/31880847
http://dx.doi.org/10.1111/ejh.13376

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7216839/
https://www.ncbi.nlm.nih.gov/pubmed/31880847
http://dx.doi.org/10.1111/ejh.13376

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