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Engraftment of human induced pluripotent stem cell-derived myogenic progenitors restores dystrophin in mice with duchenne muscular dystrophy
BACKGROUND: Duchenne muscular dystrophy (DMD) is a devastating genetic muscular disorder with no effective treatment that is caused by the loss of dystrophin. Human induced pluripotent stem cells (hiPSCs) offer a promising unlimited resource for cell-based therapies of muscular dystrophy. However, t...
Autores principales: | He, Ruojie, Li, Huan, Wang, Liang, Li, Yaqin, Zhang, Yu, Chen, Menglong, Zhu, Yuling, Zhang, Cheng |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
BioMed Central
2020
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7238630/ https://www.ncbi.nlm.nih.gov/pubmed/32430065 http://dx.doi.org/10.1186/s40659-020-00288-1 |
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