Cardiomyopathy and kidney function in agalsidase beta‐treated female Fabry patients: a pre‐treatment vs. post‐treatment analysis

AIMS: Long‐term treatment effect studies in large female Fabry patient groups are challenging to design because of phenotype heterogeneity and lack of appropriate comparison groups, and have not been reported. We compared long‐term cardiomyopathy and kidney function outcomes after agalsidase beta tr...

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Detalles Bibliográficos
Autores principales: Wanner, Christoph, Feldt‐Rasmussen, Ulla, Jovanovic, Ana, Linhart, Aleš, Yang, Meng, Ponce, Elvira, Brand, Eva, Germain, Dominique P., Hughes, Derralynn A., Jefferies, John L., Martins, Ana Maria, Nowak, Albina, Vujkovac, Bojan, Weidemann, Frank, West, Michael L., Ortiz, Alberto
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2020
Materias:
Original Research Articles
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7261571/
https://www.ncbi.nlm.nih.gov/pubmed/32100468
http://dx.doi.org/10.1002/ehf2.12647

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7261571/
https://www.ncbi.nlm.nih.gov/pubmed/32100468
http://dx.doi.org/10.1002/ehf2.12647

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