Therapeutic challenges in two adolescent male patients with Fabry disease and high antibody titres

Enzyme replacement therapy (ERT) has been shown to stabilize certain aspects of Fabry disease (FD). However, in some patients on ERT, high antibody titres have been documented, with limited clinical improvement in systemic manifestations and often with significant adverse drug reactions. We present...

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Detalles Bibliográficos
Autores principales: Mhanni, Aizeddin A., Auray-Blais, Christiane, Boutin, Michel, Johnston, Alie, LeMoine, Kaye, Patterson, Jill, Aerts, Johannes M.F.G., West, Michael L., Rockman-Greenberg, Cheryl
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Elsevier 2020
Materias:
Case Report
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7322173/
https://www.ncbi.nlm.nih.gov/pubmed/32612933
http://dx.doi.org/10.1016/j.ymgmr.2020.100618

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7322173/
https://www.ncbi.nlm.nih.gov/pubmed/32612933
http://dx.doi.org/10.1016/j.ymgmr.2020.100618

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