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High content drug screening for Fanconi anemia therapeutics

BACKGROUND: Fanconi anemia is a rare disease clinically characterized by malformations, bone marrow failure and an increased risk of solid tumors and hematologic malignancies. The only therapies available are hematopoietic stem cell transplantation for bone marrow failure or leukemia, and surgical r...

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Detalles Bibliográficos
Autores principales: Montanuy, Helena, Camps-Fajol, Cristina, Carreras-Puigvert, Jordi, Häggblad, Maria, Lundgren, Bo, Aza-Carmona, Miriam, Helleday, Thomas, Minguillón, Jordi, Surrallés, Jordi
Formato: Online Artículo Texto
Lenguaje:English
Publicado: BioMed Central 2020
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7325660/
https://www.ncbi.nlm.nih.gov/pubmed/32605631
http://dx.doi.org/10.1186/s13023-020-01437-1