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Ultrasound-assisted intrathecal injection of nusinersen in a patient with severe vertebral deformity: a case report

BACKGROUND: Spinal muscular atrophy (SMA) is a mostly autosomal recessive genetic disease characterized by progressive muscle weakness from anterior horn degeneration. Nusinersen has recently been approved as a disease-modifying drug for SMA that needs to be administered intrathecally. Its injection...

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Detalles Bibliográficos
Autores principales: Nagano, Takashi, Sakura, Shinichi, Imamachi, Noritaka, Saito, Yoji
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer Berlin Heidelberg 2020
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7419389/
https://www.ncbi.nlm.nih.gov/pubmed/32783149
http://dx.doi.org/10.1186/s40981-020-00367-y