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Gene Therapy for Hemophilia: Facts and Quandaries in the 21st Century
Therapy for hemophilia has evolved in the last 40 years from plasma-based concentrates to recombinant proteins and, more recently, to non-factor therapeutics. Along this same timeline, research in adeno-associated viral (AAV) based gene therapy vectors has provided the framework for early phase clin...
| Autores principales: | , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
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Università Cattolica del Sacro Cuore
2020
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| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7485465/ https://www.ncbi.nlm.nih.gov/pubmed/32952980 http://dx.doi.org/10.4084/MJHID.2020.069 |