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Molecular Diagnosis and Novel Therapies for Neuromuscular Diseases
With the development of novel targeted therapies, including exon skipping/inclusion and gene replacement therapy, the field of neuromuscular diseases has drastically changed in the last several years. Until 2016, there had been no FDA-approved drugs to treat Duchenne muscular dystrophy (DMD), the mo...
| Autores principales: | , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
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MDPI
2020
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| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7564006/ https://www.ncbi.nlm.nih.gov/pubmed/32947786 http://dx.doi.org/10.3390/jpm10030129 |