The SMA Clinical Trial Readiness Program: creation and evaluation of a program to enhance SMA trial readiness in the United States

Spinal muscular atrophy (SMA) is a rare neuromuscular disease with a rapidly evolving treatment landscape. To better meet the needs of trial sponsors and the patient community in the United States (US) in this evolving context, Cure SMA established a clinical trial readiness program for new and pros...

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Detalles Bibliográficos
Autores principales: Peterson, Ilse, Cruz, Rosángel, Sarr, Fatou, Stanley, Ann Marie, Jarecki, Jill
Formato: Online Artículo Texto
Lenguaje:English
Publicado: BioMed Central 2020
Materias:
Position Statement
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7564894/
https://www.ncbi.nlm.nih.gov/pubmed/32443972
http://dx.doi.org/10.1186/s13023-020-01387-8

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7564894/
https://www.ncbi.nlm.nih.gov/pubmed/32443972
http://dx.doi.org/10.1186/s13023-020-01387-8

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