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CNS-Targeting Therapies for Lysosomal Storage Diseases: Current Advances and Challenges

During the past decades, several therapeutic approaches have been developed and made rapidly available for many patients afflicted with lysosomal storage disorders (LSDs), inborn organelle disorders with broad clinical manifestations secondary to the progressive accumulation of undegraded macromolec...

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Detalles Bibliográficos
Autores principales: Edelmann, Mariola J., Maegawa, Gustavo H. B.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2020
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7693645/
https://www.ncbi.nlm.nih.gov/pubmed/33304924
http://dx.doi.org/10.3389/fmolb.2020.559804