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CNS-Targeting Therapies for Lysosomal Storage Diseases: Current Advances and Challenges
During the past decades, several therapeutic approaches have been developed and made rapidly available for many patients afflicted with lysosomal storage disorders (LSDs), inborn organelle disorders with broad clinical manifestations secondary to the progressive accumulation of undegraded macromolec...
Autores principales: | , |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Frontiers Media S.A.
2020
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Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7693645/ https://www.ncbi.nlm.nih.gov/pubmed/33304924 http://dx.doi.org/10.3389/fmolb.2020.559804 |