Deriving Vignettes for the Rare Disease AADC Deficiency Using Parent, Caregiver and Clinician Interviews to Evaluate the Impact on Health-Related Quality of Life

PURPOSE: Aromatic l-amino acid decarboxylase (AADC) deficiency is a rare genetic condition, characterised by movement disorder, and speech and cognitive functioning impairment. To enable economic evaluation of treatments, health-related quality of life or utilities need to be derived. These are curr...

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Detalles Bibliográficos
Autores principales: Hanbury, Andria, Smith, Adam B, Buesch, Katharina
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Dove 2021
Materias:
Original Research
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7800699/
https://www.ncbi.nlm.nih.gov/pubmed/33447119
http://dx.doi.org/10.2147/PROM.S278258

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7800699/
https://www.ncbi.nlm.nih.gov/pubmed/33447119
http://dx.doi.org/10.2147/PROM.S278258

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