Clinical Experience of Nusinersen in a Broad Spectrum of Spinal Muscular Atrophy: A Retrospective Study

BACKGROUND: Nusinersen has recently been approved and more widely used as first-line treatment of spinal muscular atrophy (SMA). This study aimed to evaluate the real-world experience of nusinersen use for patients with a broad spectrum of SMA. METHODS: We reviewed consecutive patients with SMA trea...

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Detalles Bibliográficos
Autores principales: Kim, Ae Ryoung, Lee, Jong-Mok, Min, Yu-Sun, Lee, Hoseok, Kim, Dongsub, Hwang, Su-Kyeong, Kwon, Soonhak, Lee, Yun Jeong
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Wolters Kluwer - Medknow 2020
Materias:
Original Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7900722/
https://www.ncbi.nlm.nih.gov/pubmed/33688130
http://dx.doi.org/10.4103/aian.AIAN_524_20

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7900722/
https://www.ncbi.nlm.nih.gov/pubmed/33688130
http://dx.doi.org/10.4103/aian.AIAN_524_20

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