Early experiences of nusinersen for the treatment of spinal muscular atrophy: Results from a large survey of patients and caregivers

BACKGROUND: This study aimed to examine the early experience of nusinersen for spinal muscular atrophy (SMA) from the patient and caregiver perspective. METHODS: A 54‐item online survey was administered to adult patients and caregivers of pediatric patients diagnosed with SMA. RESULTS: Overall, resp...

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Detalles Bibliográficos
Autores principales: Chen, Er, Dixon, Stacy, Naik, Rupali, Noone, Josh M., Buchenberger, J. Daniel, Whitmire, Sarah M., Mills, Rosalina, Arnold, William
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley & Sons, Inc. 2020
Materias:
Clinical Research Articles
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7986200/
https://www.ncbi.nlm.nih.gov/pubmed/33184859
http://dx.doi.org/10.1002/mus.27116

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7986200/
https://www.ncbi.nlm.nih.gov/pubmed/33184859
http://dx.doi.org/10.1002/mus.27116

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